Type: Neuromuscular

Duchenne Muscular Dystrophy

Duchenne Muscular Dystrophy What is Duchenne Muscular Dystrophy? Duchenne Muscular Dystrophy (DMD) is a severe genetic disorder characterized by progressive…

Spinal Muscular Atrophy

What is Spinal Muscular Atrophy? Spinal muscular atrophy (SMA) is a rare genetic neuromuscular disorder characterized by the progressive loss…

Myasthenia Gravis

What is Myasthenia Gravis? Myasthenia gravis (ORPHA code 589) is a rare autoimmune neuromuscular disorder characterized by fluctuating weakness and…