Tag: drug development
A Father’s Fight: How One Family’s Quest Is Reshaping Rare Disease Drug Development
A father's advocacy for his daughter with ultra-rare NGLY1 deficiency is reshaping how experimental gene therapies reach patients when traditional…
Multi-agent AI system accelerates clinical trial design using real-world patient data
A multi-agent AI system called EmulatRx, developed by Weill Cornell Medicine researchers, can accelerate clinical trial design by leveraging real-world…
Protein ‘Mitch’ emerges as potential obesity treatment target in human cell study
Researchers have identified a protein called Mitch that, when disabled in human cells, enhances fat metabolism and suppresses new fat…
Bacterial ‘Mix-and-Match’ Code Offers New Path to Cancer Drug Development
Researchers at the University of Warwick and Monash University have decoded how bacteria naturally synthesise multiple variants of potent anticancer…
FDA launches pilot programme to accelerate early-stage clinical trials amid global competition
The US FDA is launching a pilot programme to expedite the approval of early-stage clinical trials, citing international competitive pressures…
Experimental drug shows promise in protecting nerve cells from ALS damage
Researchers report that an experimental drug demonstrates neuroprotective properties in laboratory models of amyotrophic lateral sclerosis. The finding adds to…
Northwestern researchers identify cause of neuron overfiring in ALS and design potential treatment
Researchers at Northwestern Medicine's Les Turner ALS Center have identified the molecular mechanism driving neuronal hyperexcitability in ALS and designed…
AI Integration and Federal Policy Shape Biotech Industry Outlook at BIO 2026
Artificial intelligence and federal regulatory policy dominated discussions at BIO International Convention 2026 in San Diego. Industry leaders expressed cautious…