Tag: sickle cell disease
CRISPR Gene Therapy Shows Promise for Children with Sickle Cell Disease and Beta-Thalassemia
CRISPR gene therapy exa-cel achieved 95% efficacy in eliminating blood transfusions for children with beta-thalassemia and sickle cell disease. New…
Africa Needs Infrastructure Investment for Next-Generation Sickle Cell Therapies, BMJ Study Shows
BMJ Global Health analysis reveals African healthcare systems need major infrastructure investment to deliver next-generation gene therapies for sickle cell…
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